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Addressing Hurdles with Using Adeno-Associated Virus (AAV) Vectors in Gene Therapy
Despite many hurdles, recent advances in the use of adeno-associated virus (AAV) vectors to deliver therapeutics safely and effectively are revitalizing excitement about the possibilities of gene therapy for treating genetic diseases. Because of its nonpathogenicity, low immunogenicity, and diverse tropism to multiple cell types, AAVs have become one of the most widely used gene delivery vehicles for gene therapy. Explore various approaches to addressing AAV vector challenges, navigating the process of viral characterization, and learning how to overcome developmental hurdles in AAV-based gene therapy.
In this eBook you will learn:
- Challenges and Considerations for Developing Safe and Effective AAV Vectors for Gene Therapy
- Characterizing AAVs During Production [infographic]
- Success Stories with AAV-Based Therapeutics
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