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Advancing AAV-Based Therapies Towards Ultimate Cures
AAV-based gene therapy stands on the cusp of bringing its significant, often curative benefits not just to dozens of patients, but potentially thousands. Here, we explore five key trends for AAV gene therapies and issues in the field today, which reveal a pathway to further product approvals and more widespread adoption by healthcare systems worldwide.
We interviewed industry thought leaders in collaboration with the team at Cell & Gene Therapy Insights to provide you with the latest trends for AAV gene therapies. Read this article to learn about:
- Advances to address the targeted in vivo delivery conundrum
- Trends in overcoming safety and immunogenicity issues
- Tips for tackling chemistry, manufacturing, and controls (CMC) concerns to satisfy regulators
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